NEWS RELEASE
OCTOBER 24, 2009
  One Shot of Gene Therapy and Children with Congenital Blindness Can Now See
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Researchers from the University of Pennsylvania School of Medicine and the Center for Cellular and Molecular Therapeutics at The Children’s Hospital of Philadelphia have used gene therapy to safely improve vision in five children and seven adults with a rare form of congenital blindness.

Albert M. Maguire, M.D., associate professor of Ophthalmology at Penn and a physician at The Children's Hospital of Philadelphia; Katherine High, M.D., director of the Center for Cellular and Molecular Therapeutics at The Children's Hospital of Philadelphia; Investigator, Howard Hughes Medical Institute and Jean Bennett, M.D., Ph.D., professor of Ophthalmology, at Penn are co-authors of the reversal of blindness in children study published in The Lancet. The gene therapy vector (shown) used in the study was manufactured at the Center for Cellular and Molecular Therapeutics at The Children’s Hospital of Philadelphia.

Credit: The Children's Hospital of Philadelphia

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Albert M. Maguire, M.D., associate professor of Ophthalmology at Penn and a physician at The Children's Hospital of Philadelphia; Katherine High, M.D., director of the Center for Cellular and Molecular Therapeutics at The Children's Hospital of Philadelphia; Investigator, Howard Hughes Medical Institute and Jean Bennett, M.D., Ph.D., professor of Ophthalmology, at Penn are co-authors of the reversal of blindness in children study published in The Lancet. The gene therapy vector (shown) used in the study was manufactured at the Center for Cellular and Molecular Therapeutics at The Children’s Hospital of Philadelphia.
 


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